Therapeutic Potential of Investigational Drugs for Rett Syndrome Assessed with Behavioral Profiles in Animal Models

Mark Varney¹; Alberto Ambesi-Impiombato¹; Daniele Mazowiecki¹; Taleen Hanania¹; Frank Yucca²; Friso Postma²; Daniela Brunner^1
1PsychoGenics, Inc, Paramus, NJ; ²BioXCell, Lebanon, NH, USA.

We used data from the SmartCube® platform and in silico AI predictions to identify compounds from a screening library that may be effective in the symptomatic treatment of Rett syndrome.

References
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(Priority date 2001.)
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